Keyphrases
Senators
100%
Muscular Dystrophy
100%
RNA Toxicity
100%
Rochester
50%
Clinical Trials
50%
Small Molecules
50%
Natural History Data
25%
CUG Repeats
25%
Model Developing
25%
Transcriptome Changes
25%
Targeted Insertion
25%
National Registry
25%
Three-parallel
25%
Expanded Repeats
25%
Trial Readiness
25%
Mouse Model
25%
Protein Repeats
25%
Toxic RNA
25%
Resource Sharing
25%
Dystrophy
25%
Transcription Inhibition
25%
Early Phase Clinical Trials
25%
Post-transcriptional
25%
Effective Treatment
25%
Florida
25%
RNA Gain-of-function
25%
MBNL Proteins
25%
Clinical Methods
25%
Myotonic Dystrophy
25%
Muscle Fiber
25%
Myopathy
25%
Non-AUG Translation
25%
Therapeutic Intervention
25%
Knockdown
25%
Natural History
25%
Drug Delivery
25%
Targeted Treatment
25%
Geneticists
25%
Therapeutic Agents
25%
Genetic Mechanism
25%
Lag behind
25%
Allelic Series
25%
Medicine and Dentistry
Clinical Trial
100%
Biological Marker
100%
Muscular Dystrophy
100%
Targeted Therapy
50%
Clinical Method
50%
Therapeutic Agent
50%
Myopathy
50%
Myotonic Dystrophy
50%
Transcriptome
50%
Dystrophy
50%
Biochemistry, Genetics and Molecular Biology
RNA
100%
Animal Model
42%
Clinical Trial
28%
Small Molecule
14%
Mouse Model
14%
Genetic Mechanism
14%
Transcriptome
14%