Keyphrases
Autosomal Dominant
33%
Autosomal Dominant Retinitis pigmentosa
33%
Autosomal Recessive
33%
Bioscience
16%
Cell nucleus
16%
Cell Tropism
16%
Clinical Benefit
16%
Complementary DNA (cDNA)
83%
Current Treatment
16%
Delivery Vectors
16%
DNA Nanoparticles
16%
DNA Sequencing
16%
Effective Method
16%
Endogenous Genes
16%
Expression Cassette
16%
Expression Level
16%
Gain-of-function
16%
Gene Delivery
100%
Gene Regulation
16%
Gene Supplementation
50%
Gene Targeting
16%
Genomic DNA (gDNA)
83%
High Efficiency
16%
Host Immunity
16%
Human Population
16%
Inherited Blindness
16%
Knockdown
50%
Large Capacity
16%
Long Genes
16%
Model of Science
16%
Mouse Model
16%
Nanoparticle Systems
16%
Nanoparticles
100%
P23H
50%
Payoff
16%
Potential Gains
16%
Proof of Concept Study
16%
Quality of Life
33%
Repeated Infection
16%
Retina
16%
Retinal Diseases
16%
Retinitis pigmentosa
100%
Rhodopsin
100%
Rhodopsin Gene
50%
RNA Interference
33%
Self-compacting
16%
Severely Affected
16%
Short Hairpin RNA (shRNA)
16%
Strategy Use
16%
Subretinal Delivery
16%
Supplementation Strategies
16%
Technology Options
16%
Therapeutic Gene
16%
Therapeutic Rescue
16%
Total Loss
16%
Unique Self
16%
Viral Gene Therapy
16%
Vision Loss
16%
Visual Acuity
16%
Immunology and Microbiology
Allele
66%
Autosomal Dominant Inheritance
100%
Autosomal Recessive Inheritance
100%
Cell Nucleus
33%
Gene Control
33%
Gene Targeting
100%
Mouse Model
33%
RNAI
66%
Virus Gene
33%
Visual Acuity
33%
Wild Type
66%
Biochemistry, Genetics and Molecular Biology
Allele
28%
Autosomal Dominant Inheritance
42%
Autosomal Recessive Inheritance
42%
Expression Cassette
14%
Gene Control
14%
Gene Targeting
100%
Gene Therapy
14%
Genomics
71%
Mouse Model
14%
Retinitis pigmentosa
100%
Rhodopsin
100%
RNAI
28%
Small Hairpin RNA
14%
Visual Acuity
14%
Wild Type
28%